Rpgr-KO 基因敲除小鼠

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3. Awadh Hashem, Shaima, Georgiou, Michalis, Ali, Robin R, Michaelides, Michel. 2023. RPGR-Related Retinopathy: Clinical Features, Molecular Genetics, and Gene Replacement Therapy. In Cold Spring Harbor perspectives in medicine, 13, . doi:10.1101/cshperspect.a041280. https://pubmed.ncbi.nlm.nih.gov/37188525/

4. Gumerson, Jessica D, Alsufyani, Amal, Yu, Wenhan, Wu, Zhijian, Li, Tiansen. 2021. Restoration of RPGR expression in vivo using CRISPR/Cas9 gene editing. In Gene therapy, 29, 81-93. doi:10.1038/s41434-021-00258-6. https://pubmed.ncbi.nlm.nih.gov/34257417/