1. Dever, Daniel P, Bak, Rasmus O, Reinisch, Andreas, Weinberg, Kenneth I, Porteus, Matthew H. 2016. CRISPR/Cas9 β-globin gene targeting in human haematopoietic stem cells. In Nature, 539, 384-389. doi:10.1038/nature20134. https://pubmed.ncbi.nlm.nih.gov/27820943/
2. Di Matteo, Mario, Mátrai, Janka, Belay, Eyayu, Vandendriessche, Thierry, Chuah, Marinee K L. . PiggyBac toolbox. In Methods in molecular biology (Clifton, N.J.), 859, 241-54. doi:10.1007/978-1-61779-603-6_14. https://pubmed.ncbi.nlm.nih.gov/22367876/
3. Satterthwaite, A B, Burn, T C, Le Beau, M M, Tenen, D G. . Structure of the gene encoding CD34, a human hematopoietic stem cell antigen. In Genomics, 12, 788-94. doi:. https://pubmed.ncbi.nlm.nih.gov/1374051/
4. Grinstein, Edgar, Du, Yihua, Santourlidis, Simeon, Uhrberg, Markus, Wernet, Peter. 2007. Nucleolin regulates gene expression in CD34-positive hematopoietic cells. In The Journal of biological chemistry, 282, 12439-49. doi:. https://pubmed.ncbi.nlm.nih.gov/17255095/
5. Scherr, Michaela, Battmer, Karin, Blömer, Ulrike, Grez, Manuel, Eder, Matthias. . Lentiviral gene transfer into peripheral blood-derived CD34+ NOD/SCID-repopulating cells. In Blood, 99, 709-12. doi:. https://pubmed.ncbi.nlm.nih.gov/11781260/
6. Verma, S, Woffendin, C, Bahner, I, Kohn, D B, Nabel, G J. . Gene transfer into human umbilical cord blood-derived CD34+ cells by particle-mediated gene transfer. In Gene therapy, 5, 692-9. doi:. https://pubmed.ncbi.nlm.nih.gov/9797875/
7. Belay, Eyayu, Dastidar, Sumitava, VandenDriessche, Thierry, Chuah, Marinee K L. . Transposon-mediated gene transfer into adult and induced pluripotent stem cells. In Current gene therapy, 11, 406-13. doi:. https://pubmed.ncbi.nlm.nih.gov/21864290/
8. Cromer, M Kyle, Camarena, Joab, Martin, Renata M, Dever, Daniel P, Porteus, Matthew H. 2021. Gene replacement of α-globin with β-globin restores hemoglobin balance in β-thalassemia-derived hematopoietic stem and progenitor cells. In Nature medicine, 27, 677-687. doi:10.1038/s41591-021-01284-y. https://pubmed.ncbi.nlm.nih.gov/33737751/